Extended indication

Essential thrombocythaemia and myelofibrosis.

Therapeutic value

No estimate possible yet

Registration phase

Clinical trials

Product

Active substance

Bomedemstat

Domain

Hematology

Reason of inclusion

New medicine (specialité)

Main indication

Myeloproliferative disorders

Extended indication

Essential thrombocythaemia and myelofibrosis.

Manufacturer

Imago

Route of administration

Oral

Therapeutical formulation

Capsule

Budgetting framework

Intermural (MSZ)

Additional remarks
Lysine specific demethylase 1 inhibitor.

Registration

Registration route

Centralised (EMA)

ATMP

No

Submission date

2024

Expected Registration

2025

Orphan drug

Yes

Registration phase

Clinical trials

Therapeutic value

Therapeutic value

No estimate possible yet

Frequency of administration

1 times a day

References
NCT05223920

Expected patient volume per year

Patient volume

< 166

Market share is generally not included unless otherwise stated.

References
NKR 2018 (1);
Additional remarks
In totaal waren er 166 diagnoses in 2018 (1).

Expected cost per patient per year

There is currently nothing known about the expected cost.

Potential total cost per year

There is currently nothing known about the possible total cost.

Off label use

There is currently nothing known about off label use.

Indication extension

There is currently nothing known about indication extensions.

Other information

There is currently no futher information available.